Sickle cell disease & beta thalassemia resource center

What you and your healthcare team will need to discuss when considering gene therapy for sickle cell disease or beta thalassemia.

Recovery can take up to a year, but gene therapy has the potential to cure sickle cell disease and beta thalassemia.

An overview of the therapies used to treat sickle cell disease, including bone marrow transplants and gene therapy.

An overview of the treatments for beta thalassemia major, including stem cell transplants and gene therapy.